A developing drug has shown promising improvements with restoring effective function to neurons affected/impaired by Timothy Syndrome, also known as Long QT syndrome Type 8. This syndrome caused by a single gene mutation is responsible for impairment across multiple body functions, notably that of the heart and brain. Neurons impaired by the disorder were restored by the introduction of this new drug class, being a Antisense Oligonucleotides, These medications specifically target the expression of certain genetic disorders by modifying RNA transcripts, and effective restoration of neuron function is just one of many potential uses this drug could employ.
This drug class is incredibly promising as we scientifically discover more and more about the genetic expression and major roles regarding RNA. By studying many single-gene mutation caused disorders, modifying these drugs to specifically adapt and counteract the RNA related expression of these ailments becomes a real possibility and something to learn an incredible
amount from.
This is pretty amazing research and I have seen some work with mushrooms to repair neurons but it hasn't been scientifically proven but this development seems very promising
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